β型地中海贫血发病概况及治疗研究进展(4)
[17] Thompson AA, Walters MC, Kwiatkowski J, et al. Gene Therapy in Patients with Transfusion-Dependent β-Thalassemia[J]. New Engl J Med, 2018, 378(16): 1479-1493.[18] Cavazzana-Calvo M, Payen E, Negre O, et al. Transfusion independence and HMGA2 activation after gene therapy of human beta-thalassaemia[J]. Nature ......
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